Quality of Life and Participation in the Daily Life (Activities) of Adults with Pompe Disease Receiving Enzyme Replacement Therapy: 10 Years of International Follow-Up

Issue title: Abstracts from the 7th European Symposium on Steps Forward in Pompe Disease: Turin, Italy, November 21–22, 2014

Article type: Research Article

Authors: Güngör, D. | Kruijshaar, M.E. | Plug, I. | Rizopoulos, D. | Kanters, T.A. | Wens, S.C.A | Reuser, A.J.J | van Doorn, P.A. | van der Ploeg, A.T.

Affiliations: Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands | Department of Biostatistics, Erasmus MC University Medical Center, Rotterdam, Netherlands | Department of Health Policy and Management, Institute for Medical Technology Assessment, Erasmus University Rotterdam, Rotterdam, Netherlands | Department of Neurology, Erasmus MC University Medical Center, Rotterdam, Netherlands | Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands

Note: [] Correspondence to: A.T. van der Ploeg, Center for Lysosomal and Metabolic diseases, Erasmus MC, University Medical Center, Dr. Molewaterplein 60, Room Sb-1629, 3000 CB Rotterdam, Netherlands. E-mail: a.vanderploeg@erasmusmc.nl

DOI: 10.3233/JND-159054

Journal: Journal of Neuromuscular Diseases, vol. 2, no. s1, pp. S63-S63, 2015