Immunological Factors in Pompe Disease Management: Clinical Experience and Implications for Newborn Screening

Issue title: Abstracts from the 7th European Symposium on Steps Forward in Pompe Disease: Turin, Italy, November 21–22, 2014

Article type: Research Article

Authors: Kishnani, Priya S. | Kazi, Zoheb B. | Berrier, Kathryn L. | Dearmey, Stephanie M. | Bali, Deeksha S. | Rosenberg, Amy S.

Affiliations: Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC | Division of Therapeutic Proteins, Office of Biotechnology Products, Center for Drug Evaluation and Research, United States Food and Drug Administration

Note: [] Correspondence to: Priya S. Kishnani, MD, Duke University Medical Center, GSRB1 Box 103856, 4th floor, 905 S. LaSalle Street, Durham, North Carolina 27710, USA, Tel.: +1 919 684-2036; Fax: +1 919 668-8944. E-mail: priya.kishnani@duke.edu

DOI: 10.3233/JND-159007

Journal: Journal of Neuromuscular Diseases, vol. 2, no. s1, pp. S7-S7, 2015